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Comment
. 2020 Nov 12;383(20):1989.
doi: 10.1056/NEJMc2026458.

Givosiran for Acute Intermittent Porphyria

Elena Gomá-Garcés  1 , M Vanessa Pérez-Gómez  1 , Alberto Ortíz  1
Affiliations
Comment

Givosiran for Acute Intermittent Porphyria

Elena Gomá-Garcés et al. N Engl J Med. .
No abstract available

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  • Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
    Balwani M, Sardh E, Ventura P, Peiró PA, Rees DC, Stölzel U, Bissell DM, Bonkovsky HL, Windyga J, Anderson KE, Parker C, Silver SM, Keel SB, Wang JD, Stein PE, Harper P, Vassiliou D, Wang B, Phillips J, Ivanova A, Langendonk JG, Kauppinen R, Minder E, Horie Y, Penz C, Chen J, Liu S, Ko JJ, Sweetser MT, Garg P, Vaishnaw A, Kim JB, Simon AR, Gouya L; ENVISION Investigators. Balwani M, et al. N Engl J Med. 2020 Jun 11;382(24):2289-2301. doi: 10.1056/NEJMoa1913147. N Engl J Med. 2020. PMID: 32521132 Clinical Trial.

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