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. 2020 Jun;16(2):200016.
doi: 10.1183/20734735.0016-2020.

The era of CFTR modulators: improvements made and remaining challenges

Sara Cuevas-Ocaña  1 , Onofrio Laselva  2   3 , Julie Avolio  4 , Raffaella Nenna  5
Affiliations

The era of CFTR modulators: improvements made and remaining challenges

Sara Cuevas-Ocaña et al. Breathe (Sheff). 2020 Jun.

Abstract

The entry into the clinic of CFTR modulators such as TRIKAFTA has significantly improved life for ∼90% CF patients carrying one or two F508del mutations but challenges remain for rare CFTR mutations and the management of lung infections @SaraOcana1 https://bit.ly/3aRafQF.

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Conflict of interest statement

Conflict of interest: S. Cuevas-Ocaña has nothing to disclose. Conflict of interest: O. Laselva has nothing to disclose. Conflict of interest: J. Avolio has nothing to disclose. Conflict of interest: R. Nenna has nothing to disclose.

References

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