Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation
Comment
. 2021 Feb;27(2):202-204.
doi: 10.1038/s41591-021-01235-7.

A plethora of gene therapies for hemoglobinopathies

Cynthia E Dunbar  1
Affiliations
Comment

A plethora of gene therapies for hemoglobinopathies

Cynthia E Dunbar. Nat Med. 2021 Feb.
No abstract available

PubMed Disclaimer

Comment on

  • CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
    Frangoul H, Altshuler D, Cappellini MD, Chen YS, Domm J, Eustace BK, Foell J, de la Fuente J, Grupp S, Handgretinger R, Ho TW, Kattamis A, Kernytsky A, Lekstrom-Himes J, Li AM, Locatelli F, Mapara MY, de Montalembert M, Rondelli D, Sharma A, Sheth S, Soni S, Steinberg MH, Wall D, Yen A, Corbacioglu S. Frangoul H, et al. N Engl J Med. 2021 Jan 21;384(3):252-260. doi: 10.1056/NEJMoa2031054. Epub 2020 Dec 5. N Engl J Med. 2021. PMID: 33283989 Clinical Trial.

References

    1. Frangoul, H. et al. N. Engl. J. Med. https://doi.org/10.1056/NEJMoa2031054 (2020).
    1. Dunbar, C. E. et al. Science 359, eaan4672 (2018). - DOI
    1. Fischer, A. & Hacein-Bey-Abina, S. J. Exp. Med. 217, e20190607 (2020). - DOI
    1. Fitzhugh, C. D. et al. Blood 130, 1946–1948 (2017). - DOI
    1. Naldini, L., Trono, D. & Verma, I. M. Science 353, 1101–1102 (2016). - DOI

Publication types

LinkOut - more resources