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. 2020 Dec 11;117(50):868-869.
doi: 10.3238/arztebl.2020.0868.

The Evaluation of Orphan Drugs by the German Joint Federal Committee-An Eight-Year Review

Sandra Schulz  1 , Anna Marie Passon, Matthias Perleth, Michael Kulig, Nina Paschke, Katja Matthias
Affiliations

The Evaluation of Orphan Drugs by the German Joint Federal Committee-An Eight-Year Review

Sandra Schulz et al. Dtsch Arztebl Int. .
No abstract available

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Figures

Figure
Figure
Flow chart of (a) the ODs included in the analysis, and (b) their additional benefit classification OD, orphan drugs; TIs, therapeutic indications
See this image and copyright information in PMC

References

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    1. Gemeinsamer Bundesausschuss. Verfahren der Nutzenbewertung nach § 35a SGB V. www.g-ba.de/bewertungsverfahren/nutzenbewertung/ (last accessed on 1 April 2020)
    1. Vokinger KN, Kesselheim AS. Application of orphan drug designation to cancer treatments (2008-2017): a comprehensive and comparative analysis of the USA and EU. BMJ Open. 2019;9 e028634. - PMC - PubMed
    1. Sarpatwari A, Kesselheim AS. Reforming the orphan drug act for the 21st Century. N Engl J Med. 2019;381:106–108. - PubMed
    1. Europäische Kommission. Proposal for a regulation of the European Parliament and of the Council on health technology assessment and amending directive 2011/24/EU. www.ec.europa.eu/health/sites/health/files/technology_assessment/docs/co... (last accessed on 4 June 2020)