Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation
. 2021 Jun;39(6):671-677.
doi: 10.1038/s41587-021-00945-0.

A call to arms against ultra-rare diseases

Affiliations

A call to arms against ultra-rare diseases

Stanley T Crooke. Nat Biotechnol. 2021 Jun.
No abstract available

PubMed Disclaimer

References

    1. Nguengang Wakap, S. et al. Eur. J. Hum. Genet. 28, 165–173 (2020). - DOI
    1. Jo, A. et al. BMJ Open 9, e027248 (2019). - DOI
    1. Copley-Merriman, K. Value Health 21, 491–492 (2018). - DOI
    1. Richter, T. et al. Value Health 18, 906–914 (2015). - DOI
    1. Crooke, S. T., Seth, P. P., Vickers, T. A. & Liang, X. H. J. Am. Chem. Soc. 142, 14754–14771 (2020). - DOI

MeSH terms

Substances

LinkOut - more resources