Maybe too much of a good thing in gene therapy
- PMID: 34131327
- DOI: 10.1038/s41593-021-00882-w
Maybe too much of a good thing in gene therapy
Comment on
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Gain of toxic function by long-term AAV9-mediated SMN overexpression in the sensorimotor circuit.Nat Neurosci. 2021 Jul;24(7):930-940. doi: 10.1038/s41593-021-00827-3. Epub 2021 Apr 1. Nat Neurosci. 2021. PMID: 33795885 Free PMC article.
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