EBMT/ESID inborn errors working party guidelines for hematopoietic stem cell transplantation for inborn errors of immunity

Affiliations

¹ Willem-Alexander Children's Hospital, Pediatric Stem Cell Transplantation Program, Leiden University Medical Center, Leiden, The Netherlands. a.lankester@lumc.nl.
² Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, LMU, Munich, Germany.
³ Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health, London, UK.
⁴ Translational and Clinical Research Institute, Newcastle University, and Paediatric Haematopoietic Stem Cell Transplant Unit, Great North Children's Hospital, Newcastle upon Tyne, UK.
⁵ Department of Hematology, Oncology, Immunology, Gene-therapy and Stem Cell Transplantation, and Children's Research Center (CRC), University Children's Hospital, ZurichZurich, Switzerland.
⁶ Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
⁷ Institute of Immunity and Transplantation, University College London Hospitals NHS FT and Royal Free London Hospitals NHS FT, London, UK.
⁸ Unité d'immune-Hematologie et Rhumatologie Pédiatrique, Hôpital Necker Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
⁹ Université de Paris, Paris, France.
¹⁰ Institut Imagine, INSERM UMR1163, Laboratory of genomic Dynamics in the Immune system, Paris, France.
¹¹ Institut Imagine, INSERM UMR1163, Laboratory of Immunogenetics of Pediatric Autoimmune Diseases, Paris, France.

Review

A C Lankester et al. Bone Marrow Transplant. 2021 Sep.

. 2021 Sep;56(9):2052-2062.

doi: 10.1038/s41409-021-01378-8. Epub 2021 Jul 5.

¹ Willem-Alexander Children's Hospital, Pediatric Stem Cell Transplantation Program, Leiden University Medical Center, Leiden, The Netherlands. a.lankester@lumc.nl.
² Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, LMU, Munich, Germany.
³ Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health, London, UK.
⁴ Translational and Clinical Research Institute, Newcastle University, and Paediatric Haematopoietic Stem Cell Transplant Unit, Great North Children's Hospital, Newcastle upon Tyne, UK.
⁵ Department of Hematology, Oncology, Immunology, Gene-therapy and Stem Cell Transplantation, and Children's Research Center (CRC), University Children's Hospital, ZurichZurich, Switzerland.
⁶ Department of Pediatrics, University Medical Center Ulm, Ulm, Germany.
⁷ Institute of Immunity and Transplantation, University College London Hospitals NHS FT and Royal Free London Hospitals NHS FT, London, UK.
⁸ Unité d'immune-Hematologie et Rhumatologie Pédiatrique, Hôpital Necker Enfants Malades, Assistance Publique-Hôpitaux de Paris, Paris, France.
⁹ Université de Paris, Paris, France.
¹⁰ Institut Imagine, INSERM UMR1163, Laboratory of genomic Dynamics in the Immune system, Paris, France.
¹¹ Institut Imagine, INSERM UMR1163, Laboratory of Immunogenetics of Pediatric Autoimmune Diseases, Paris, France.

No abstract available

Conflict of interest statement

The authors declare no competing interests.

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