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Comment
. 2021 Oct;8(10):2094-2095.
doi: 10.1002/acn3.51459. Epub 2021 Sep 21.

The need for evidence-based treatment decisions in spinal muscular atrophy type 0

Yasemin Erbas  1 , Nicole Gusset  1
Affiliations
Comment

The need for evidence-based treatment decisions in spinal muscular atrophy type 0

Yasemin Erbas et al. Ann Clin Transl Neurol. 2021 Oct.
No abstract available

PubMed Disclaimer

Conflict of interest statement

N.G. is an advisor and lecturer for Biogen, Novartis, Novartis Gene Therapies (AveXis) and Roche.

Comment in

Comment on

  • Nusinersen in type 0 spinal muscular atrophy: should we treat?
    Tiberi E, Costa S, Pane M, Priolo F, de Sanctis R, Romeo D, Tiziano FD, Conti G, Vento G, Mercuri E. Tiberi E, et al. Ann Clin Transl Neurol. 2020 Dec;7(12):2481-2483. doi: 10.1002/acn3.51126. Epub 2020 Nov 4. Ann Clin Transl Neurol. 2020. PMID: 33147378 Free PMC article.

References

    1. Tiberi E, Costa S, Pane M, et al. Nusinersen in type 0 spinal muscular atrophy: should we treat? Ann Clin Transl Neurol. 2000;7(12):2481‐2483. - PMC - PubMed
    1. Glascock J, Sampson J, Haidet‐Phillips A, et al. Treatment algorithm for infants diagnosed with spinal muscular atrophy through newborn screening. J Neuromuscul Dis. 2018;5(2):145‐158. - PMC - PubMed

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