Reply to: The need for evidence-based treatment decisions in spinal muscular atrophy type 0

Affiliations

¹ Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
² Pediatric Neurology, Università Cattolica del Sacro Cuore, Rome, Italy.
³ Neonatology Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
⁴ Institute of Genetics, Università Cattolica del Sacro Cuore, Rome, Italy.
⁵ Pediatric Intensive Care Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.

Comment

Eugenio Mercuri et al. Ann Clin Transl Neurol. 2021 Oct.

. 2021 Oct;8(10):2093.

doi: 10.1002/acn3.51458. Epub 2021 Sep 21.

¹ Centro Clinico Nemo, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
² Pediatric Neurology, Università Cattolica del Sacro Cuore, Rome, Italy.
³ Neonatology Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.
⁴ Institute of Genetics, Università Cattolica del Sacro Cuore, Rome, Italy.
⁵ Pediatric Intensive Care Unit, Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome, Italy.

No abstract available

Comment on

Nusinersen in type 0 spinal muscular atrophy: should we treat?
Tiberi E, Costa S, Pane M, Priolo F, de Sanctis R, Romeo D, Tiziano FD, Conti G, Vento G, Mercuri E. Tiberi E, et al. Ann Clin Transl Neurol. 2020 Dec;7(12):2481-2483. doi: 10.1002/acn3.51126. Epub 2020 Nov 4. Ann Clin Transl Neurol. 2020. PMID: 33147378 Free PMC article.
The need for evidence-based treatment decisions in spinal muscular atrophy type 0.
Erbas Y, Gusset N. Erbas Y, et al. Ann Clin Transl Neurol. 2021 Oct;8(10):2094-2095. doi: 10.1002/acn3.51459. Epub 2021 Sep 21. Ann Clin Transl Neurol. 2021. PMID: 34546649 Free PMC article. No abstract available.

1. Erbas J, Gusset N. The need for evidence based treatment decisions in spinal muscular atrophy type 0. Ann Clin Transl Neurol. - PMC - PubMed
1. Tiberi E, Costa S, Pane M, et al. Nusinersen in type 0 spinal muscular atrophy: should we treat? Ann Clin Transl Neurol. 2020;7:2481‐2483. - PMC - PubMed