Gene Therapy Updates in Achromatopsia
- PMID: 34584052
- DOI: 10.1097/IIO.0000000000000379
Gene Therapy Updates in Achromatopsia
Conflict of interest statement
The author declares that there is no conflicts of interest to disclose.
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- Zobor D, Werner A, Stanzial F, et al. The clinical phenotype of CNGA3-related achromatopsia: pretreatment characterization in preparation of a gene replacement therapy trial. Investig Ophthalmol Vis Sci. 2017;58:821–832.
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