When deficient lysosomes make the liver fatty and the arteries greasy: How to treat, whom and when?
- PMID: 34915053
- DOI: 10.1016/j.jhep.2021.12.002
When deficient lysosomes make the liver fatty and the arteries greasy: How to treat, whom and when?
Conflict of interest statement
Conflict of interest FL reports consulting fees and honoraria from Alexion. Please refer to the accompanying ICMJE disclosure form for further details.
Comment on
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A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency.N Engl J Med. 2015 Sep 10;373(11):1010-20. doi: 10.1056/NEJMoa1501365. N Engl J Med. 2015. PMID: 26352813 Clinical Trial.
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Sebelipase alfa in children and adults with lysosomal acid lipase deficiency: Final results of the ARISE study.J Hepatol. 2022 Mar;76(3):577-587. doi: 10.1016/j.jhep.2021.10.026. Epub 2021 Nov 10. J Hepatol. 2022. PMID: 34774639
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