Risdiplam: new opportunities but more to be done
- PMID: 34942130
- DOI: 10.1016/S1474-4422(21)00428-2
Risdiplam: new opportunities but more to be done
Conflict of interest statement
I serve in advisory boards for Roche, Biogen, and Novartis, providing intellectual and teaching activities. I did not take part in any of the risdiplam trials.
Comment in
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Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial.Lancet Neurol. 2022 Jan;21(1):42-52. doi: 10.1016/S1474-4422(21)00367-7. Lancet Neurol. 2022. PMID: 34942136
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