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Comment
. 2022 Mar;28(3):171-172.
doi: 10.1016/j.molmed.2022.01.005. Epub 2022 Jan 24.

Bringing gene therapy to where it's needed

Stefan Radtke  1 , Hans-Peter Kiem  2
Affiliations
Comment

Bringing gene therapy to where it's needed

Stefan Radtke et al. Trends Mol Med. 2022 Mar.

Abstract

Gene editing allows the precise modification of cells to correct genetic defects or enhance immunotherapies. A limitation is the delivery of this technology to specific cells or organs. Recently, Banskota et al. reported the use of virus-like particles (VLPs) loaded with gene-editing agents for gene therapy delivery directly inside the body.

Keywords: base editors; gene therapy; in vivo delivery; target specificity.

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Conflict of interest statement

Declaration of interests No interests are declared.

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