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. 2022 Mar;54(3):219-222.
doi: 10.1038/s41588-022-01027-w.

A call for an integrated approach to improve efficiency, equity and sustainability in rare disease research in the United States

Meghan C Halley  1 , Hadley Stevens Smith  2 , Euan A Ashley  3 , Aaron J Goldenberg #  4 , Holly K Tabor #  5   6
Affiliations

A call for an integrated approach to improve efficiency, equity and sustainability in rare disease research in the United States

Meghan C Halley et al. Nat Genet. 2022 Mar.

Abstract

To build a more efficient, equitable, and sustainable approach to rare disease research in the United States, we must prioritize integrated research infrastructure and approaches that focus on understanding connections across rare diseases.

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Conflict of interest statement

Competing Interests Statement

E.A.A. is a Non-Executive Director at AstraZeneca. The other authors declare no competing interests.

Comment in

  • Rare diseases, common challenges.
    [No authors listed] [No authors listed] Nat Genet. 2022 Mar;54(3):215. doi: 10.1038/s41588-022-01037-8. Nat Genet. 2022. PMID: 35288710 No abstract available.

References

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