Gene therapy for Friedreich ataxia: Too much, too little, or just right?

Affiliations

Editorial

R Mark Payne. Mol Ther Methods Clin Dev. 2022.

. 2022 Mar 4:25:1-2.

doi: 10.1016/j.omtm.2022.02.008. eCollection 2022 Jun 9.

¹ Indiana University School of Medicine, Wells Center for Pediatric Research, 1044 West Walnut, R4302b, Indianapolis, IN 46202, USA.

No abstract available

Conflict of interest statement

R.M.P. is a paid consultant for Larimar Therapeutics, Inc., which had no input or knowledge of this work.

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