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Comment
. 2022 Jun 9;386(23):2247.
doi: 10.1056/NEJMc2204934.

Gene Therapy for Hemophilia A

Affiliations
Comment

Gene Therapy for Hemophilia A

Madhusudana G Sanal et al. N Engl J Med. .
No abstract available

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Comment in

  • Gene Therapy for Hemophilia A. Reply.
    Ozelo MC, Wong WY. Ozelo MC, et al. N Engl J Med. 2022 Jun 9;386(23):2247. doi: 10.1056/NEJMc2204934. N Engl J Med. 2022. PMID: 35675187 No abstract available.

Comment on

  • Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A.
    Ozelo MC, Mahlangu J, Pasi KJ, Giermasz A, Leavitt AD, Laffan M, Symington E, Quon DV, Wang JD, Peerlinck K, Pipe SW, Madan B, Key NS, Pierce GF, O'Mahony B, Kaczmarek R, Henshaw J, Lawal A, Jayaram K, Huang M, Yang X, Wong WY, Kim B; GENEr8-1 Trial Group. Ozelo MC, et al. N Engl J Med. 2022 Mar 17;386(11):1013-1025. doi: 10.1056/NEJMoa2113708. N Engl J Med. 2022. PMID: 35294811 Clinical Trial.

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