Mitapivat versus Placebo for Pyruvate Kinase Deficiency
- PMID: 35767453
- DOI: 10.1056/NEJMc2206275
Mitapivat versus Placebo for Pyruvate Kinase Deficiency
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Mitapivat versus Placebo for Pyruvate Kinase Deficiency. Reply.N Engl J Med. 2022 Jun 30;386(26):2539. doi: 10.1056/NEJMc2206275. N Engl J Med. 2022. PMID: 35767454 No abstract available.
Comment on
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Mitapivat versus Placebo for Pyruvate Kinase Deficiency.N Engl J Med. 2022 Apr 14;386(15):1432-1442. doi: 10.1056/NEJMoa2116634. N Engl J Med. 2022. PMID: 35417638 Clinical Trial.
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