Mitapivat for treatment of pyruvate kinase deficiency
- PMID: 35988547
- DOI: 10.1016/S2352-3026(22)00249-6
Mitapivat for treatment of pyruvate kinase deficiency
Conflict of interest statement
I received fees for consultancy work and honoraria from Novartis and consultancy work from Global Blood Therapeutics. I acknowledge N Conran and D B Costa for their help with writing the manuscript.
Comment on
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Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial.Lancet Haematol. 2022 Oct;9(10):e724-e732. doi: 10.1016/S2352-3026(22)00214-9. Epub 2022 Aug 18. Lancet Haematol. 2022. PMID: 35988546 Clinical Trial.
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