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. 2022 Dec;21(12):1065-1066.
doi: 10.1016/S1474-4422(22)00427-6. Epub 2022 Oct 14.

New results for risdiplam in spinal muscular atrophy

Susan T Iannaccone  1
Affiliations
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New results for risdiplam in spinal muscular atrophy

Susan T Iannaccone. Lancet Neurol. 2022 Dec.
No abstract available

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Conflict of interest statement

SI receives partial salary support from NIH Wellstone Muscular Dystrophy Center (P50HD087351), NeuroNEXT (U24NS107176), and the Muscular Dystrophy Association. She receives research support from the DoD W81XWH2010293, Parent Project for MD, CureSMA and industry (Capricor, RegenXBio, Novartis, Biogen, Sarepta, PTC Therapeutics, Scholar Rock, FibroGen and ReveraGen). She has served on Medical Advisory Boards for Novartis, Biogen, and Sarepta and as a consultant for Genentech.

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