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. 2023 Mar;29(3):518-519.
doi: 10.1038/s41591-023-02208-8.

Access to gene therapy for rare diseases when commercialization is not fit for purpose

Thomas Fox  1 , Juan Bueren  2 , Fabio Candotti  3 , Alain Fischer  4 , Alessandro Aiuti  5 , Arjan Lankester  6 ; AGORA Initiative; Claire Booth  7
Collaborators, Affiliations

Access to gene therapy for rare diseases when commercialization is not fit for purpose

Thomas Fox et al. Nat Med. 2023 Mar.
No abstract available

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References

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    1. Amaral, M. D. Curr. Opin. Pharmacol. 63, 102201 (2022). - DOI - PubMed
    1. Ferrua, F. et al. Hum. Gene Ther. 28, 972–981 (2017). - DOI - PubMed

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