Gene therapy for SCID, now up to 3!

Affiliations

¹ Pediatric Hematology-Immunology and Rheumatology Department, Hôpital Necker-Enfants Malades, AP-HP Centre Université de Paris, Paris, France; Institut Imagine, INSERM UMR 1163, Paris, France; Collège de France, Paris, France. Electronic address: alain.fischer@aphp.fr.
² Pediatric Hematology-Immunology and Rheumatology Department, Hôpital Necker-Enfants Malades, AP-HP Centre Université de Paris, Paris, France; Université Paris-Cité, Imagine Institute, Laboratory of Immunogenetics of Pediatric 2, Autoimmunity, INSERM UMR 1163, Paris, France.

Editorial

Alain Fischer et al. J Allergy Clin Immunol. 2023 May.

. 2023 May;151(5):1255-1256.

doi: 10.1016/j.jaci.2023.02.015. Epub 2023 Feb 23.

¹ Pediatric Hematology-Immunology and Rheumatology Department, Hôpital Necker-Enfants Malades, AP-HP Centre Université de Paris, Paris, France; Institut Imagine, INSERM UMR 1163, Paris, France; Collège de France, Paris, France. Electronic address: alain.fischer@aphp.fr.
² Pediatric Hematology-Immunology and Rheumatology Department, Hôpital Necker-Enfants Malades, AP-HP Centre Université de Paris, Paris, France; Université Paris-Cité, Imagine Institute, Laboratory of Immunogenetics of Pediatric 2, Autoimmunity, INSERM UMR 1163, Paris, France.

No abstract available

Keywords: Gene therapy.

Comment on

Lentiviral Gene Therapy for Artemis-Deficient SCID.
Cowan MJ, Yu J, Facchino J, Fraser-Browne C, Sanford U, Kawahara M, Dara J, Long-Boyle J, Oh J, Chan W, Chag S, Broderick L, Chellapandian D, Decaluwe H, Golski C, Hu D, Kuo CY, Miller HK, Petrovic A, Currier R, Hilton JF, Punwani D, Dvorak CC, Malech HL, McIvor RS, Puck JM. Cowan MJ, et al. N Engl J Med. 2022 Dec 22;387(25):2344-2355. doi: 10.1056/NEJMoa2206575. N Engl J Med. 2022. PMID: 36546626 Free PMC article. Clinical Trial.