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. 2023 Mar;193(1):5-6.
doi: 10.1002/ajmg.c.32039.

Note from the editors

Tiina K Urv  1 , Melissa A Parisi  2
Affiliations

Note from the editors

Tiina K Urv et al. Am J Med Genet C Semin Med Genet. 2023 Mar.
No abstract available

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References

REFERENCES

    1. Brooks, P. J., Urv, T. K., & Parisi, M. A. (2023). Gene-targeted therapies: Overview and implications. American Journal of Medical Genetics Part C: Seminars in Medical Genetics, 193(1), 13-18. https://doi.org/10.1002/ajmg.c.32033
    1. Garrison, L. P., Lo, A. W., Finkel, R. S., & Deverka, P. A. (2023). A review of economic issues for gene-targeted therapies: Value, affordability, and access. American Journal of Medical Genetics Part C: Seminars in Medical Genetics, 193(1), 64-76. https://doi.org/10.1002/ajmg.c.32037
    1. Gaviglio, A. M., Skinner, M. W., Lou, L. J., Finkel, R. S., Augustine, E. F., & Goldenberg, A. J. (2023). Gene-targeted therapies: Towards equitable development, diagnosis, and access. American Journal of Medical Genetics. Part C, Seminars in Medical Genetics, 193(1), 56-63. https://doi.org/10.1002/ajmg.c.32032
    1. Lekstrom-Himes, J., Augustine, E. F., Brower, A., Defay, T., Finkel, R. S., McGuire, A. L., … Yu, T. W. (2023). Data sharing to advance gene-targeted therapies in rare diseases. American Journal of Medical Genetics. Part C, Seminars in Medical Genetics, 193(1), 87-98. https://doi.org/10.1002/ajmg.c.32028
    1. Lekstrom-Himes, J., Brooks, P. J., Koeberl, D. D., Brower, A., Goldenberg, A., Green, R. C., … Augustine, E. F. (2023). Moving away from one disease at a time: Screening, trial design, and regulatory implications of novel platform technologies. American Journal of Medical Genetics Part C: Seminars in Medical Genetics, 193(1), 30-43. https://doi.org/10.1002/ajmg.c.32031

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