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Comment
. 2023 May;22(5):353.
doi: 10.1038/d41573-023-00057-1.

Base editing treats SMA in mice

M Teresa Villanueva
Comment

Base editing treats SMA in mice

M Teresa Villanueva. Nat Rev Drug Discov. 2023 May.
No abstract available

Keywords: Biotechnology; Drug discovery; Gene therapy; Genetics; Therapeutics.

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Comment on

  • Base editing rescue of spinal muscular atrophy in cells and in mice.
    Arbab M, Matuszek Z, Kray KM, Du A, Newby GA, Blatnik AJ, Raguram A, Richter MF, Zhao KT, Levy JM, Shen MW, Arnold WD, Wang D, Xie J, Gao G, Burghes AHM, Liu DR. Arbab M, et al. Science. 2023 Apr 21;380(6642):eadg6518. doi: 10.1126/science.adg6518. Epub 2023 Apr 14. Science. 2023. PMID: 36996170 Free PMC article.

References

    1. Arbab, M. et al. Base editing rescue of spinal muscular atrophy in cells and in mice. Science https://doi.org/10.1126/science.adg6518 (2023)

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