Correcting the aberrant Fanconi anemia transcriptional program by gene therapy

Affiliations

¹ Genetics and Genome Biology, Research Institute, The Hospital for Sick Children, Toronto, Ontario; Institute of Medical Science, Faculty of Medicine, University of Toronto; Division of Haematology/Oncology, Department of Paediatrics, The Hospital for Sick Children and University of Toronto, Ontario. yigal.dror@sickkids.ca.

Editorial

Yigal Dror. Haematologica. 2023.

. 2023 Oct 1;108(10):2566-2567.

doi: 10.3324/haematol.2023.283031.

¹ Genetics and Genome Biology, Research Institute, The Hospital for Sick Children, Toronto, Ontario; Institute of Medical Science, Faculty of Medicine, University of Toronto; Division of Haematology/Oncology, Department of Paediatrics, The Hospital for Sick Children and University of Toronto, Ontario. yigal.dror@sickkids.ca.

No abstract available

Comment on

Gene therapy restores the transcriptional program of hematopoietic stem cells in Fanconi anemia.
Lasaga M, Río P, Vilas-Zornoza A, Planell N, Navarro S, Alignani D, Fernández-Varas B, Mouzo D, Zubicaray J, Pujol RM, Nicoletti E, Schwartz JD, Sevilla J, Ainciburi M, Ullate-Agote A, Surrallés J, Perona R, Sastre L, Prosper F, Gomez-Cabrero D, Bueren JA. Lasaga M, et al. Haematologica. 2023 Oct 1;108(10):2652-2663. doi: 10.3324/haematol.2022.282418. Haematologica. 2023. PMID: 37021532 Free PMC article.

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