Gene silencing on a WHIM
- PMID: 37410507
- DOI: 10.1182/blood.2023020478
Gene silencing on a WHIM
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CRISPR/Cas9-mediated Cxcr4 disease allele inactivation for gene therapy in a mouse model of WHIM syndrome.Blood. 2023 Jul 6;142(1):23-32. doi: 10.1182/blood.2022019142. Blood. 2023. PMID: 36928087 Free PMC article.
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