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. 2023 Oct;108(5):347-350.
doi: 10.1136/archdischild-2023-325359. Epub 2023 Jul 9.

Gene therapy for spinal muscular atrophy

Vasantha Lakshmi Gowda  1 , Heinz Jungbluth  2   3 , Elizabeth Wraige  2
Affiliations

Gene therapy for spinal muscular atrophy

Vasantha Lakshmi Gowda et al. Arch Dis Child Educ Pract Ed. 2023 Oct.
No abstract available

Keywords: Neurology; Paediatrics; Pharmacology; Therapeutics.

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Conflict of interest statement

Competing interests: VLG has received consultancy/speaker honoraria from Novartis, Roche, Biogen, PTC Therapeutics, Pfizer and Sarepta Therapeutics. EW has received consultancy/speaker honoraria from Pfizer, Biogen and Novartis. HJ has received consultancy/honoraria from Pfizer.

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