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Comment

. 2023 Sep;22(9):693.

doi: 10.1038/d41573-023-00124-7.

Creating a path to splice-switching ASO therapies

PMID: 37528209
DOI: 10.1038/d41573-023-00124-7

Comment

Creating a path to splice-switching ASO therapies

Katie Kingwell. Nat Rev Drug Discov. 2023 Sep.

. 2023 Sep;22(9):693.

doi: 10.1038/d41573-023-00124-7.

Author

PMID: 37528209
DOI: 10.1038/d41573-023-00124-7

No abstract available

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Comment on

A framework for individualized splice-switching oligonucleotide therapy.
Kim J, Woo S, de Gusmao CM, Zhao B, Chin DH, DiDonato RL, Nguyen MA, Nakayama T, Hu CA, Soucy A, Kuniholm A, Thornton JK, Riccardi O, Friedman DA, El Achkar CM, Dash Z, Cornelissen L, Donado C, Faour KNW, Bush LW, Suslovitch V, Lentucci C, Park PJ, Lee EA, Patterson A, Philippakis AA, Margus B, Berde CB, Yu TW. Kim J, et al. Nature. 2023 Jul;619(7971):828-836. doi: 10.1038/s41586-023-06277-0. Epub 2023 Jul 12. Nature. 2023. PMID: 37438524 Free PMC article.

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References

1. Kim, J. et al. A framework for individualized splice-switching oligonucleotide therapy. Nature 619, 828–836 (2023) - PubMed - DOI - PMC

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