BioMarin's ROCTAVIAN Wins Food and Drug Administration Approval As First Gene Therapy for Severe Hemophilia A
- PMID: 37590493
- DOI: 10.1089/hum.2023.29251.bfs
BioMarin's ROCTAVIAN Wins Food and Drug Administration Approval As First Gene Therapy for Severe Hemophilia A
Publication types
MeSH terms
LinkOut - more resources
Full Text Sources
Medical
Research Materials
