How early is too early? Diagnosis of tuberous sclerosis complex in a neonate
- PMID: 37675664
- PMCID: PMC10846816
- DOI: 10.4103/jpgm.jpgm_326_23
How early is too early? Diagnosis of tuberous sclerosis complex in a neonate
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- French JA, Lawson JA, Yapici Z, Ikeda H, Polster T, Nabbout R, et al. Adjunctive everolimus therapy for treatment-resistant focal-onset seizures associated with tuberous sclerosis (EXIST-3): A phase 3, randomised, double-blind, placebo-controlled study. Lancet. 2016;388:2153–63. - PubMed
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