Targeting expanded trinucleotide repeats

Comment

Sarah Crunkhorn. Nat Rev Drug Discov. 2023 Nov.

. 2023 Nov;22(11):873.

doi: 10.1038/d41573-023-00160-3.

No abstract available

Comment on

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1. Ikenoshita, S. et al. A cyclic pyrrole-imidazole polyamide reduces pathogenic RNA in CAG/CTG triplet repeat neurological disease models. J. Clin. Invest. https://doi.org/10.1172/JCI164792 (2023)