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. 2023 Oct;29(10):2391-2392.
doi: 10.1038/s41591-023-02459-5.

First regulatory qualification of a digital primary endpoint to measure treatment efficacy in DMD

Laurent Servais  1   2 , Damien Eggenspieler  3 , Margaux Poleur  4 , Marc Grelet  3 , Francesco Muntoni  5 , Paul Strijbos  6 , Mélanie Annoussamy  3
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Free article

First regulatory qualification of a digital primary endpoint to measure treatment efficacy in DMD

Laurent Servais et al. Nat Med. 2023 Oct.
Free article
No abstract available

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References

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    1. Muntoni, F. et al. PLoS ONE 14, e0221097 (2019). - DOI - PubMed - PMC
    1. Muntoni, F. et al. Neuromuscul. Disord. 32, 271–283 (2022). - DOI - PubMed
    1. Pane, M. et al. J. Pediatr. 161, 705–709.e701 (2012). - DOI - PubMed

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