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. 2023 Dec;22(12):937-938.
doi: 10.1038/d41573-023-00168-9.

IRDiRC Drug Repurposing Guidebook: making better use of existing drugs to tackle rare diseases

Anneliene Hechtelt Jonker, Simon Day, Michela Gabaldo, Heather Stone, Martin de Kort, Daniel J O'Connor, Anna Maria Gerdina Pasmooij

IRDiRC Drug Repurposing Guidebook: making better use of existing drugs to tackle rare diseases

Anneliene Hechtelt Jonker et al. Nat Rev Drug Discov. 2023 Dec.
No abstract available

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References

    1. Dawkins, H. J. S. et al. Progress in Rare Diseases Research 2010–2016: An IRDiRC Perspective. Clin. Transl. Sci. 11, 11–20 (2018). - PubMed - DOI
    1. Fang, H. et al. FDALabel for drug repurposing studies and beyond. Nat. Biotechnol. 38, 1378–1379 (2020). - PubMed - DOI
    1. Austin, C. P., Mount, B. A. & Colvis, C. M. Envisioning an actionable research agenda to facilitate repurposing of off-patent drugs. Nat. Rev. Drug Discov. 20, 723–724 (2021). - PubMed - DOI
    1. Hechtelt Jonker, A. et al. Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook. Nat. Rev. Drug Discov. 19, 495–496 (2020). - PubMed - DOI

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