Myelodysplasia and transgene inactivation in X-CGD-γ retroviral gene therapy: The usual suspects and new players

. 2023 Dec 6;31(12):3367-3368.

doi: 10.1016/j.ymthe.2023.11.007. Epub 2023 Nov 18.

Affiliations

¹ Infection, Immunity, and Inflammation Teaching and Research Department, Great Ormond Street Institute of Child Health, University College London, London, UK.
² Infection, Immunity, and Inflammation Teaching and Research Department, Great Ormond Street Institute of Child Health, University College London, London, UK. Electronic address: g.santilli@ucl.ac.uk.

Thomas E Whittaker et al. Mol Ther. 2023.

. 2023 Dec 6;31(12):3367-3368.

doi: 10.1016/j.ymthe.2023.11.007. Epub 2023 Nov 18.

¹ Infection, Immunity, and Inflammation Teaching and Research Department, Great Ormond Street Institute of Child Health, University College London, London, UK.
² Infection, Immunity, and Inflammation Teaching and Research Department, Great Ormond Street Institute of Child Health, University College London, London, UK. Electronic address: g.santilli@ucl.ac.uk.

No abstract available

Conflict of interest statement

Declaration of interests The authors declare no competing interests.

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