Affiliations

• ¹ Institut national de la santé et de la recherche médicale, Marseille Medical Genetics, U1251, Aix Marseille University, Marseille, France.
• ² Division of Child Neurology, Department of Pediatrics, University of Texas Southwestern, Dallas, TX, United States.
• ³ Center for Alzheimer's and Neurodegenerative Diseases, University of Texas Southwestern, Dallas, TX, United States.
• ⁴ Center for Gene Therapy, Abigail Wexner Research Institute at Nationwide Children's Hospital, Columbus, OH, United States.
• ⁵ Department of Pediatrics, The Ohio State University, Columbus, OH, United States.
• ⁶ Center for Duchenne Muscular Dystrophy at UCLA, Los Angeles, CA, United States.
• ⁷ Department of Microbiology, Immunology and Molecular Genetics, David Geffen School of Medicine, College of Letters and Sciences, University of California, Los Angeles, Los Angeles, CA, United States.