Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy. Reply
- PMID: 38055269
- DOI: 10.1056/NEJMc2312288
Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy. Reply
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Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy.N Engl J Med. 2023 Sep 28;389(13):1203-1210. doi: 10.1056/NEJMoa2307798. N Engl J Med. 2023. PMID: 37754285 Free PMC article.