Iptacopan and danicopan for paroxysmal nocturnal hemoglobinuria
- PMID: 38824627
- PMCID: PMC11145001
- DOI: 10.18553/jmcp.2024.30.6.618
Iptacopan and danicopan for paroxysmal nocturnal hemoglobinuria
References
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- Hillmen P, Szer J, Weitz I, et al. . Pegcetacoplan versus eculizumab in paroxysmal nocturnal hemoglobinuria. N Engl J Med. 2021;384(11):1028-37. doi:10.1056/NEJMoa2029073 - PubMed
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- Socié G, Mary JY, de Gramont A, et al.; French Society of Haematology. Paroxysmal nocturnal haemoglobinuria: Long-term follow-up and prognostic factors. Lancet. 1996;348(9027):573-7. doi:10.1016/S0140-6736(95)12360-1 - PubMed
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- Hill A, Hillmen PJ, Smith A, et al. . The incidence and prevalence of Paroxysmal Nocturnal Hemoglobinuria (PNH) and survival of patients in Yorkshire. Blood. 2006;108(11):985. doi:10.1182/blood.V108.11.985.985
