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. 2024 Jun;56(6):1472-1473.
doi: 10.1038/s12276-024-01247-6. Epub 2024 Jun 3.

Catching up but still miles behind-a patient registry for otoferlin

Barbara Vona  1   2 , Bernd Wollnik  1   3 , Nicola Strenzke  2   4 , Tobias Moser  5   6   7
Affiliations

Catching up but still miles behind-a patient registry for otoferlin

Barbara Vona et al. Exp Mol Med. 2024 Jun.
No abstract available

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Conflict of interest statement

The authors declare no competing interests.

References

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    1. Lv, J. et al. AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial. Lancet. 10.1016/S0140-6736(23)02874-X (2024). - PubMed
    1. Qi, J. et al. AAV-mediated gene therapy restores hearing in patients with DFNB9 deafness. Adv. Sci. (Weinh). 10.1002/advs.202306788 (2024). - PMC - PubMed
    1. World Health Organization. World Report on Hearing (World Health Organization, 2021). - PMC - PubMed
    1. Morton, C. C. & Nance, W. E. Newborn hearing screening—a silent revolution. N. Engl. J. Med.354, 2151–2164 (2006). 10.1056/NEJMra050700 - DOI - PubMed

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