Cystic Fibrosis Transmembrane Conductance Regulator Modulators: Real-World Evidence Highlights Need for Worldwide Access
- PMID: 38949605
- PMCID: PMC11284316
- DOI: 10.1513/AnnalsATS.202404-439ED
Cystic Fibrosis Transmembrane Conductance Regulator Modulators: Real-World Evidence Highlights Need for Worldwide Access
Comment on
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Multisystemic Effects of Elexacaftor-Tezacaftor-Ivacaftor in Adults with Cystic Fibrosis and Advanced Lung Disease.Ann Am Thorac Soc. 2024 Jul;21(7):1053-1064. doi: 10.1513/AnnalsATS.202312-1065OC. Ann Am Thorac Soc. 2024. PMID: 38579175
References
-
- Kessler WR, Andersen DH. Heat prostration in fibrocystic disease of the pancreas and other conditions. Pediatrics . 1951;8:648–656. - PubMed
-
- Burgel PR, Paillasseur JL, Durieu I, Reynaud-Gaubert M, Hamidfar R, Murris-Espin M, et al. Multisystemic effects of elexacaftor–tezacaftor–ivacaftor in adults with cystic fibrosis and advanced lung disease Ann Am Thorac Soc 2024211053–1064.. - PubMed
-
- Martin C, Reynaud-Gaubert M, Hamidfar R, Durieu I, Murris-Espin M, Danner-Boucher I, et al. Sustained effectiveness of elexacaftor-tezacaftor-ivacaftor in lung transplant candidates with cystic fibrosis. J Cyst Fibros . 2022;21:489–496. - PubMed
-
- Burgel PR, Durieu I, Chiron R, Ramel S, Danner-Boucher I, Prevotat A, et al. French Cystic Fibrosis Reference Network Study Group Rapid improvement after starting elexacaftor-tezacaftor-ivacaftor in patients with cystic fibrosis and advanced pulmonary disease. Am J Respir Crit Care Med . 2021;204:64–73. - PubMed
-
- Daines CL, Tullis E, Costa S, Linnemann RW, Mall MA, McKone EF, et al. VX17-445-105 Study Group Long-term safety and efficacy of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis and at least one F508del allele: 144-week interim results from a 192-week open-label extension study. Eur Respir J . 2023;62:2202029. - PMC - PubMed
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