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Editorial
. 2024 Dec 15;210(12):1387-1389.
doi: 10.1164/rccm.202408-1516ED.

The Road Less Traveled: Slow but Steady Progress Toward Cystic Fibrosis Gene Therapy by the UK Respiratory Gene Therapy Consortium

Terence R Flotte  1
Affiliations
Editorial

The Road Less Traveled: Slow but Steady Progress Toward Cystic Fibrosis Gene Therapy by the UK Respiratory Gene Therapy Consortium

Terence R Flotte. Am J Respir Crit Care Med. .
No abstract available

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Figures

Figure 1.
Figure 1.
Timeline of the UK Respiratory Gene Therapy Consortium. Milestones in CF gene therapy product development are described in the boxes aligned to the various years. Created with BioRender based on information from the UK Respiratory Gene Therapy Consortium website (8). CF = cystic fibrosis.
See this image and copyright information in PMC

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References

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    1. Flotte T, Carter B, Conrad C, Guggino W, Reynolds T, Rosenstein B, et al. A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease. Hum Gene Ther . 1996;7:1145–1159. - PubMed

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