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. 2024 Dec 1;81(12):1239-1240.
doi: 10.1001/jamaneurol.2024.3331.

Barriers to Tofersen Therapy for Variant SOD1-Mediated ALS

Stanley H Appel  1 , Jason R Thonhoff  1
Affiliations

Barriers to Tofersen Therapy for Variant SOD1-Mediated ALS

Stanley H Appel et al. JAMA Neurol. .
No abstract available

Plain language summary

This Viewpoint advocates for the accelerated adoption of tofersen therapy to treat patients with variant SOD1-mediated amyotrophic lateral sclerosis (ALS) and describes the current barriers to treatment.

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