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. 2024 Dec 4;32(12):4172-4174.
doi: 10.1016/j.ymthe.2024.10.030. Epub 2024 Nov 13.

R-loops facilitate AAV-mediated nuclease-free gene targeting

Affiliations

R-loops facilitate AAV-mediated nuclease-free gene targeting

Bryan Hu et al. Mol Ther. .
No abstract available

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Conflict of interest statement

Declaration of interests D.D. is a member of the scientific advisory board for Solid Biosciences and an equity holder of Solid Biosciences, a member of the scientific advisory board for Sardocor Corp., and an inventor of several issued and filed patents on Duchenne muscular dystrophy gene therapy and AAV vectors. R.H. has been serving as a member of scientific advisory boards for Pfizer and is the recipient of research funding from Roche.

References

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