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. 2024 Oct 30;35(4):102364.
doi: 10.1016/j.omtn.2024.102364. eCollection 2024 Dec 10.

A drug candidate for a rare polyalanine disease targeting the protein quality control

Sharon Pochtar  1   2 , Avraham Ashkenazi  1   2
Affiliations

A drug candidate for a rare polyalanine disease targeting the protein quality control

Sharon Pochtar et al. Mol Ther Nucleic Acids. .
No abstract available

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Conflict of interest statement

The authors declare no competing interests.

Figures

Figure 1
Figure 1
Potential mode of action of vorinostat (SAHA) on protein quality control mechanisms targeting mutant PHOX2B in cell and mouse models of CCHS
See this image and copyright information in PMC

References

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