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Review

GENE MANIPULATION

Franco Locatelli  1   2 , Mattia Algeri  1   3
A.T. Taher  1 , D. Farmakis  2 , J.B. Porter  3 , M.D. Cappellini  4 , K.M. Musallam  5
, editors.
In: Guidelines for the Management of Transfusion-Dependent β-Thalassaemia (TDT) [Internet]. 5th edition. Nicosia, Cyprus: Thalassaemia International Federation; 2025. Chapter 15.
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Review

GENE MANIPULATION

Franco Locatelli et al.
Free Books & Documents
No abstract available

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Conflict of interest statement

FL reports participating in speaker’s bureau with Amgen, Bristol Myers Squibb, Miltenyi Biotec, Neovii, Novartis, SOBI and Vertex Pharmaceuticals; and consultancy for Sanofi, Vertex Pharmaceuticals and Amgen; and honoraria, advisory board participation for Amgen. MA reports scientific advisory board and steering committee participation for Vertex Pharmaceuticals. All competing interests are outside the present work.

References

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    1. Bulcha JT, Wang Y, Ma H, Tai PWL, Gao G Viral vector platforms within the gene therapy landscape. Signal Transduct Target Ther. 2021;6(1):53. - PMC - PubMed
    1. Ferrari G, Thrasher AJ, Aiuti A Gene therapy using haematopoietic stem and progenitor cells. Nat Rev Genet. 2021;22(4):216–234. - PubMed

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