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Review
. 2025 Jun 26.
doi: 10.1007/s00439-025-02758-6. Online ahead of print.

Efficacy of delandistrogene moxeparvovec on Duchenne muscular dystrophy: a systematic review and meta-analysis

Carlos Pascual-Morena  1   2 , Silvana Patiño-Cardona  1 , Irene Martínez-García  3 , Jaime Fernández-Bravo-Rodrigo  4 , Miriam Garrido-Miguel  1   2
Affiliations
Review

Efficacy of delandistrogene moxeparvovec on Duchenne muscular dystrophy: a systematic review and meta-analysis

Carlos Pascual-Morena et al. Hum Genet. .
No abstract available

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Conflict of interest statement

Declarations. Competing interests: The authors declare no competing interests.

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References

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    1. Alfano LN, Lowes LP, Berry KM et al (2014) T.P.1: pilot study evaluating motivation on the performance of timed walking in boys with Duchenne muscular dystrophy. Neuromuscul Disord 24:860. https://doi.org/10.1016/j.nmd.2014.06.224 - DOI
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