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. 2025 Sep;13(9):102553.
doi: 10.1016/j.jchf.2025.102553. Epub 2025 Jul 7.

Using Patient-Reported Outcomes to Assess Transthyretin Amyloid Cardiomyopathy Progression in Patients Treated With Disease-Modifying Therapy

Juliana C Levy  1 , Dimitrios Bampatsias  1 , Alfonsina Mirabal Santos  1 , Sergio Teruya  1 , Karan Wats  1 , Mathew S Maurer  2
Affiliations

Using Patient-Reported Outcomes to Assess Transthyretin Amyloid Cardiomyopathy Progression in Patients Treated With Disease-Modifying Therapy

Juliana C Levy et al. JACC Heart Fail. 2025 Sep.
No abstract available

Keywords: ATTR-CM; EQ-5D-5L; KCCQ; QOL; disease progression.

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Conflict of interest statement

Funding Support and Author Disclosures Dr Maurer has received grants from the National Institutes of Health (R01HL139671 and R01AG081582-01); has received consulting income from Eidos, Prothena, Ionis, Alnylam, Novo Nordisk, and Intellia; and has received institutional support in the form of clinical trial funding from Pfizer, Attralus, Ionis, Eidos, Intellia, Alexion, and Alnylam. All other authors have reported that they have no relationships relevant to the contents of this paper to disclose.

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