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. 2025 Aug 21;393(8):830.
doi: 10.1056/NEJMc2509703.

AAV Gene Therapy in Severe Hemophilia B. Reply

Ulrike M Reiss  1 , Andrew M Davidoff  1 , Amit C Nathwani  2
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AAV Gene Therapy in Severe Hemophilia B. Reply

Ulrike M Reiss et al. N Engl J Med. .
No abstract available

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  • Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B.
    Reiss UM, Davidoff AM, Tuddenham EGD, Chowdary P, McIntosh J, Muczynski V, Journou M, Simini G, Ireland L, Mohamed S, Riddell A, Pie AJ, Hall A, Quaglia A, Mangles S, Mahlangu J, Haley K, Recht M, Shen YM, Halka KG, Fortner G, Morton CL, Gu Z, Hayden RT, Neufeld EJ, Okhomina VI, Kang G, Nathwani AC. Reiss UM, et al. N Engl J Med. 2025 Jun 12;392(22):2226-2234. doi: 10.1056/NEJMoa2414783. N Engl J Med. 2025. PMID: 40499172 Free PMC article. Clinical Trial.

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