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. 2025 Oct 12.
doi: 10.1111/bjh.70203. Online ahead of print.

Primary CD34+ cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243

Daniel Nowak  1 , Marie Demmerle  1 , Alessa Klär  1 , Alexander Streuer  1 , Vladimir Riabov  1 , Eva Altrock  1 , Felicitas Rapp  1 , Ann-Christin Belzer  1 , Teresa Klink  1 , Meret Hahn  1 , Franziska Hofmann  1 , Verena Nowak  1 , Nadine Weimer  1 , Julia Obländer  1 , Iris Palme  1 , Melda Göl  1 , Ali Darwich  2 , Laurenz Steiner  1 , Mohammed Abba  1 , Georgia Metzgeroth  1 , Wolf-Karsten Hofmann  1 , Nanni Schmitt  1
Affiliations

Primary CD34+ cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243

Daniel Nowak et al. Br J Haematol. .
No abstract available

Keywords: MDS; TAK‐243; VEXAS syndrome; pevonedistat.

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References

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