Case Reports
Bone marrow transplantation in Gaucher's disease: effect of mixed chimeric state
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- PMID: 7994251
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Case Reports
Bone marrow transplantation in Gaucher's disease: effect of mixed chimeric state
Bone Marrow Transplant.
1994 Aug.
Abstract
The effective dose and schedule of enzyme replacement therapy for Gaucher's disease have not been definitely established. We report a case of mixed chimeric state in an allogeneic BMT patient and followed her clinical and laboratory progress. The result shows that a low but sustained glucocerebrosidase level may provide symptomatic relief for this lysosomal disorder.
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