Evaluation of subretinally delivered Cas9 ribonucleoproteins in murine and porcine animal models highlights key considerations for therapeutic translation of genetic medicines.
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Wei SC, et al. Among authors: cantor aj.
PLoS One. 2025 Jun 24;20(6):e0317387. doi: 10.1371/journal.pone.0317387. eCollection 2025.
PLoS One. 2025.
PMID: 40554553
Free PMC article.