Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Results by year

Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1968 1
1969 2
1974 1
1977 1
1979 2
1980 2
1981 3
1982 1
1983 1
1984 3
1985 1
1986 1
1992 1
1998 1
2003 1
2006 1
2007 5
2008 1
2010 2
2011 1
2013 2
2014 3
2016 2
2017 4
2018 4
2019 3
2020 5
2021 3
2022 3
2023 1
2024 7
2025 6

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

69 results

Results by year

Filters applied: . Clear all
Page 1
Intrathecal Gene Therapy for Giant Axonal Neuropathy.
Bharucha-Goebel DX, Todd JJ, Saade D, Norato G, Jain M, Lehky T, Bailey RM, Chichester JA, Calcedo R, Armao D, Foley AR, Mohassel P, Tesfaye E, Carlin BP, Seremula B, Waite M, Zein WM, Huryn LA, Crawford TO, Sumner CJ, Hoke A, Heiss JD, Charnas L, Hooper JE, Bouldin TW, Kang EM, Rybin D, Gray SJ, Bönnemann CG; GAN Trial Team. Bharucha-Goebel DX, et al. Among authors: bailey rm. N Engl J Med. 2024 Mar 21;390(12):1092-1104. doi: 10.1056/NEJMoa2307952. N Engl J Med. 2024. PMID: 38507752 Free PMC article.
Editorial: Personalized medicine for neuromuscular disorders.
Bartoli M, Bailey RM, Meyer K, Barthélémy F. Bartoli M, et al. Among authors: bailey rm. Front Cell Dev Biol. 2023 Nov 16;11:1329048. doi: 10.3389/fcell.2023.1329048. eCollection 2023. Front Cell Dev Biol. 2023. PMID: 38033860 Free PMC article. No abstract available.
Gene Transfer Therapy for Neurodevelopmental Disorders.
Ozlu C, Bailey RM, Sinnett S, Goodspeed KD. Ozlu C, et al. Among authors: bailey rm. Dev Neurosci. 2021;43(3-4):230-240. doi: 10.1159/000515434. Epub 2021 Apr 21. Dev Neurosci. 2021. PMID: 33882495 Review.
SLC13A5 Deficiency Disorder: From Genetics to Gene Therapy.
Goodspeed K, Liu JS, Nye KL, Prasad S, Sadhu C, Tavakkoli F, Bilder DA, Minassian BA, Bailey RM. Goodspeed K, et al. Among authors: bailey rm. Genes (Basel). 2022 Sep 15;13(9):1655. doi: 10.3390/genes13091655. Genes (Basel). 2022. PMID: 36140822 Free PMC article. Review.
Evaluating scenarios toward zero plastic pollution.
Lau WWY, Shiran Y, Bailey RM, Cook E, Stuchtey MR, Koskella J, Velis CA, Godfrey L, Boucher J, Murphy MB, Thompson RC, Jankowska E, Castillo Castillo A, Pilditch TD, Dixon B, Koerselman L, Kosior E, Favoino E, Gutberlet J, Baulch S, Atreya ME, Fischer D, He KK, Petit MM, Sumaila UR, Neil E, Bernhofen MV, Lawrence K, Palardy JE. Lau WWY, et al. Among authors: bailey rm. Science. 2020 Sep 18;369(6510):1455-1461. doi: 10.1126/science.aba9475. Epub 2020 Jul 23. Science. 2020. PMID: 32703909 Free article.
Gene Therapy: Novel Approaches to Targeting Monogenic Epilepsies.
Goodspeed K, Bailey RM, Prasad S, Sadhu C, Cardenas JA, Holmay M, Bilder DA, Minassian BA. Goodspeed K, et al. Among authors: bailey rm. Front Neurol. 2022 Jun 21;13:805007. doi: 10.3389/fneur.2022.805007. eCollection 2022. Front Neurol. 2022. PMID: 35847198 Free PMC article. Review.
Developmental phenotype and quality of life in SLC13A5 citrate transporter disorder.
Ozlu C, Adams RM, Solidum RM, Cooper S, Best CR, Elacio J, Kavanaugh BC, Spelbrink EM, Brown TL, Nye K, Liu JS, Bailey RM, Goodspeed K, Porter BE. Ozlu C, et al. Among authors: bailey rm. Dev Med Child Neurol. 2025 Jul;67(7):930-940. doi: 10.1111/dmcn.16218. Epub 2024 Dec 22. Dev Med Child Neurol. 2025. PMID: 39710583
Methods for gene transfer to the central nervous system.
Kantor B, Bailey RM, Wimberly K, Kalburgi SN, Gray SJ. Kantor B, et al. Among authors: bailey rm. Adv Genet. 2014;87:125-97. doi: 10.1016/B978-0-12-800149-3.00003-2. Adv Genet. 2014. PMID: 25311922 Free PMC article. Review.
Sleep Abnormalities in SLC13A5 Citrate Transporter Disorder.
Adams RM, Ozlu C, Bailey LE, Solidum RM, Cooper S, Best CR, Elacio J, Kavanaugh BC, Brown TL, Nye K, Liu J, Porter BE, Goodspeed K, Bailey RM. Adams RM, et al. Among authors: bailey rm. Genes (Basel). 2024 Oct 18;15(10):1338. doi: 10.3390/genes15101338. Genes (Basel). 2024. PMID: 39457462 Free PMC article.
69 results